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10-Q Filing

REGENXBIO INC. CIK: 1590877 Q1 2023
Filing Information
Form Type 10-Q
Accession Number 0000950170-23-017200
Period End Date 20230331
Filing Date 20230503
Fiscal Year 2023
Fiscal Period Q1
XBRL Instance rgnx-20230331_htm.xml
Filing Contents
Balance Sheet 80 line items
Line Item Tag Value Unit Period
Preferred stock, par value PreferredStockParOrStatedValuePerShare $0.00 USD Point-in-time
Preferred stock, par value PreferredStockParOrStatedValuePerShare $0.00 USD Point-in-time
Preferred stock, shares authorized PreferredStockSharesAuthorized 10.00M shares Point-in-time
Preferred stock, shares authorized PreferredStockSharesAuthorized 10.00M shares Point-in-time
Preferred stock, shares issued PreferredStockSharesIssued 0.00 shares Point-in-time
Cash and cash equivalents CashAndCashEquivalentsAtCarryingValue $191.87M USD Point-in-time
Cash and cash equivalents CashAndCashEquivalentsAtCarryingValue $96.95M USD Point-in-time
Cash and cash equivalents CashAndCashEquivalentsAtCarryingValue $70.09M USD Point-in-time
Preferred stock, shares issued PreferredStockSharesIssued 0.00 shares Point-in-time
Preferred stock, shares outstanding PreferredStockSharesOutstanding 0.00 shares Point-in-time
Marketable securities MarketableSecuritiesCurrent $267.69M USD Point-in-time
Preferred stock, shares outstanding PreferredStockSharesOutstanding 0.00 shares Point-in-time
Marketable securities MarketableSecuritiesCurrent $261.73M USD Point-in-time
Common stock, par value CommonStockParOrStatedValuePerShare $0.00 USD Point-in-time
Accounts receivable AccountsReceivableNetCurrent $28.08M USD Point-in-time
Common stock, par value CommonStockParOrStatedValuePerShare $0.00 USD Point-in-time
Accounts receivable AccountsReceivableNetCurrent $18.86M USD Point-in-time
Common stock, shares authorized CommonStockSharesAuthorized 100.00M shares Point-in-time
Prepaid expenses PrepaidExpenseCurrent $13.90M USD Point-in-time
Prepaid expenses PrepaidExpenseCurrent $15.52M USD Point-in-time
Common stock, shares authorized CommonStockSharesAuthorized 100.00M shares Point-in-time
Common stock, shares issued CommonStockSharesIssued 43.30M shares Point-in-time
Other current assets OtherAssetsCurrent $9.35M USD Point-in-time
Other current assets OtherAssetsCurrent $23.00M USD Point-in-time
Common stock, shares issued CommonStockSharesIssued 43.47M shares Point-in-time
Total current assets AssetsCurrent $415.98M USD Point-in-time
Common stock, shares outstanding CommonStockSharesOutstanding 43.30M shares Point-in-time
Total current assets AssetsCurrent $389.20M USD Point-in-time
Common stock, shares outstanding CommonStockSharesOutstanding 43.47M shares Point-in-time
Marketable securities MarketableSecuritiesNoncurrent $141.71M USD Point-in-time
Marketable securities MarketableSecuritiesNoncurrent $200.56M USD Point-in-time
Accounts receivable, net AccountsReceivableNetNoncurrent $1.50M USD Point-in-time
Accounts receivable, net AccountsReceivableNetNoncurrent $1.30M USD Point-in-time
Property and equipment, net PropertyPlantAndEquipmentNet $141.69M USD Point-in-time
Property and equipment, net PropertyPlantAndEquipmentNet $141.57M USD Point-in-time
Operating lease right-of-use assets OperatingLeaseRightOfUseAsset $65.12M USD Point-in-time
Operating lease right-of-use assets OperatingLeaseRightOfUseAsset $63.73M USD Point-in-time
Restricted cash RestrictedCashAndCashEquivalentsNoncurrent $2.03M USD Point-in-time
Restricted cash RestrictedCashAndCashEquivalentsNoncurrent $2.03M USD Point-in-time
Restricted cash RestrictedCashAndCashEquivalentsNoncurrent $2.03M USD Point-in-time
Other assets OtherAssetsNoncurrent $8.29M USD Point-in-time
Other assets OtherAssetsNoncurrent $6.40M USD Point-in-time
Total assets Assets $747.83M USD Point-in-time
Total assets Assets $833.27M USD Point-in-time
Accounts payable AccountsPayableCurrent $23.28M USD Point-in-time
Accounts payable AccountsPayableCurrent $27.21M USD Point-in-time
Accrued expenses and other current liabilities AccruedExpensesAndOtherCurrentLiabilities $46.79M USD Point-in-time
Accrued expenses and other current liabilities AccruedExpensesAndOtherCurrentLiabilities $31.71M USD Point-in-time
Deferred revenue ContractWithCustomerLiabilityCurrent $1.31M USD Point-in-time
Deferred revenue ContractWithCustomerLiabilityCurrent $1.83M USD Point-in-time
Operating lease liabilities OperatingLeaseLiabilityCurrent $6.00M USD Point-in-time
Operating lease liabilities OperatingLeaseLiabilityCurrent $6.30M USD Point-in-time
Liability related to sale of future royalties LiabilityRelatedToSaleOfFutureRoyaltiesCurrent $49.73M USD Point-in-time
Liability related to sale of future royalties LiabilityRelatedToSaleOfFutureRoyaltiesCurrent $48.60M USD Point-in-time
Total current liabilities LiabilitiesCurrent $130.43M USD Point-in-time
Total current liabilities LiabilitiesCurrent $112.33M USD Point-in-time
Operating lease liabilities OperatingLeaseLiabilityNoncurrent $88.80M USD Point-in-time
Operating lease liabilities OperatingLeaseLiabilityNoncurrent $86.99M USD Point-in-time
Liability related to sale of future royalties LiabilityRelatedToSaleOfFutureRoyaltiesNonCurrent $89.00M USD Point-in-time
Liability related to sale of future royalties LiabilityRelatedToSaleOfFutureRoyaltiesNonCurrent $77.38M USD Point-in-time
Other liabilities OtherLiabilitiesNoncurrent $5.98M USD Point-in-time
Other liabilities OtherLiabilitiesNoncurrent $8.83M USD Point-in-time
Total liabilities Liabilities $282.69M USD Point-in-time
Total liabilities Liabilities $317.07M USD Point-in-time
Preferred stock; $0.0001 par value; 10,000 shares authorized, no shares issued and outstanding at March 31, 2023 and December 31, 2022 PreferredStockValue - USD Point-in-time
Preferred stock; $0.0001 par value; 10,000 shares authorized, no shares issued and outstanding at March 31, 2023 and December 31, 2022 PreferredStockValue - USD Point-in-time
Common stock; $0.0001 par value; 100,000 shares authorized at March 31, 2023 and December 31, 2022; 43,465 and 43,299 shares issued and outstanding at March 31, 2023 and December 31, 2022, respectively CommonStockValue $4.00K USD Point-in-time
Common stock; $0.0001 par value; 100,000 shares authorized at March 31, 2023 and December 31, 2022; 43,465 and 43,299 shares issued and outstanding at March 31, 2023 and December 31, 2022, respectively CommonStockValue $4.00K USD Point-in-time
Additional paid-in capital AdditionalPaidInCapitalCommonStock $984.99M USD Point-in-time
Additional paid-in capital AdditionalPaidInCapitalCommonStock $973.14M USD Point-in-time
Accumulated other comprehensive loss AccumulatedOtherComprehensiveIncomeLossNetOfTax $-11.62M USD Point-in-time
Accumulated other comprehensive loss AccumulatedOtherComprehensiveIncomeLossNetOfTax $-15.40M USD Point-in-time
Accumulated deficit RetainedEarningsAccumulatedDeficit $-441.55M USD Point-in-time
Accumulated deficit RetainedEarningsAccumulatedDeficit $-508.23M USD Point-in-time
Total stockholders equity StockholdersEquity $689.67M USD Point-in-time
Total stockholders equity StockholdersEquity $516.20M USD Point-in-time
Total stockholders equity StockholdersEquity $764.30M USD Point-in-time
Total stockholders equity StockholdersEquity $465.14M USD Point-in-time
Total liabilities and stockholders equity LiabilitiesAndStockholdersEquity $747.83M USD Point-in-time
Total liabilities and stockholders equity LiabilitiesAndStockholdersEquity $833.27M USD Point-in-time
Income Statement 41 line items
Line Item Tag Value Unit Period
Revenues RevenueFromContractWithCustomerExcludingAssessedTax $19.14M USD 1 Quarter
Revenues RevenueFromContractWithCustomerExcludingAssessedTax $22.22M USD 1 Quarter
Cost of revenues CostOfGoodsAndServicesSold $4.11M USD 1 Quarter
Cost of revenues CostOfGoodsAndServicesSold $15.72M USD 1 Quarter
Research and development ResearchAndDevelopmentExpense $55.63M USD 1 Quarter
Research and development ResearchAndDevelopmentExpense $58.52M USD 1 Quarter
General and administrative GeneralAndAdministrativeExpense $22.32M USD 1 Quarter
General and administrative GeneralAndAdministrativeExpense $22.63M USD 1 Quarter
Other operating expenses OtherOperatingExpenses $83.00K USD 1 Quarter
Other operating expenses OtherOperatingExpenses $33.00K USD 1 Quarter
Total operating expenses CostsAndExpenses $85.30M USD 1 Quarter
Total operating expenses CostsAndExpenses $93.75M USD 1 Quarter
Loss from operations OperatingIncomeLoss $-66.16M USD 1 Quarter
Loss from operations OperatingIncomeLoss $-71.53M USD 1 Quarter
Interest income from licensing InterestIncomeFromLicencing $70.00K USD 1 Quarter
Interest income from licensing InterestIncomeFromLicencing $94.00K USD 1 Quarter
Investment income InvestmentIncomeNet $799.00K USD 1 Quarter
Investment income InvestmentIncomeNet $2.17M USD 1 Quarter
Interest expense InterestExpense $6.13M USD 1 Quarter
Interest expense InterestExpense $2.75M USD 1 Quarter
Total other income (expense) NonoperatingIncomeExpense $-519.00K USD 1 Quarter
Total other income (expense) NonoperatingIncomeExpense $-5.24M USD 1 Quarter
Loss before income taxes IncomeLossFromContinuingOperationsBeforeIncomeTaxesExtraordinaryItemsNoncontrollingInterest $-66.68M USD 1 Quarter
Loss before income taxes IncomeLossFromContinuingOperationsBeforeIncomeTaxesExtraordinaryItemsNoncontrollingInterest $-76.76M USD 1 Quarter
Income Tax Benefit IncomeTaxExpenseBenefit $-41.00K USD 1 Quarter
Net loss NetIncomeLoss $-66.68M USD 1 Quarter
Net loss NetIncomeLoss $-76.72M USD 1 Quarter
Unrealized gain (loss) on available-for-sale securities, net OtherComprehensiveIncomeUnrealizedHoldingGainLossOnSecuritiesArisingDuringPeriodNetOfTax $-9.38M USD 1 Quarter
Unrealized gain (loss) on available-for-sale securities, net OtherComprehensiveIncomeUnrealizedHoldingGainLossOnSecuritiesArisingDuringPeriodNetOfTax $3.78M USD 1 Quarter
Total other comprehensive income (loss) OtherComprehensiveIncomeLossNetOfTax $-9.38M USD 1 Quarter
Total other comprehensive income (loss) OtherComprehensiveIncomeLossNetOfTax $3.78M USD 1 Quarter
Comprehensive loss ComprehensiveIncomeNetOfTax $-86.10M USD 1 Quarter
Comprehensive loss ComprehensiveIncomeNetOfTax $-62.90M USD 1 Quarter
Net loss per share, basic EarningsPerShareBasic $-1.79 USD 1 Quarter
Net loss per share, basic EarningsPerShareBasic $-1.53 USD 1 Quarter
Net loss per share, diluted EarningsPerShareDiluted $-1.53 USD 1 Quarter
Net loss per share, diluted EarningsPerShareDiluted $-1.79 USD 1 Quarter
Weighted-average common shares outstanding, basic WeightedAverageNumberOfSharesOutstandingBasic 43,451.00 shares 1 Quarter
Weighted-average common shares outstanding, basic WeightedAverageNumberOfSharesOutstandingBasic 42,944.00 shares 1 Quarter
Weighted-average common shares outstanding, diluted WeightedAverageNumberOfDilutedSharesOutstanding 43,451.00 shares 1 Quarter
Weighted-average common shares outstanding, diluted WeightedAverageNumberOfDilutedSharesOutstanding 42,944.00 shares 1 Quarter
Cash Flow Statement 62 line items
Line Item Tag Value Unit Period
Net loss ProfitLoss $-76.72M USD 1 Quarter
Net loss ProfitLoss $-66.68M USD 1 Quarter
Stock-based compensation expense ShareBasedCompensation $10.80M USD 1 Quarter
Stock-based compensation expense ShareBasedCompensation $11.21M USD 1 Quarter
Depreciation and amortization DepreciationAndAmortization $4.18M USD 1 Quarter
Depreciation and amortization DepreciationAndAmortization $2.59M USD 1 Quarter
Net amortization of premiums on marketable debt securities AccretionAmortizationOfDiscountsAndPremiumsInvestments $-682.00K USD 1 Quarter
Net amortization of premiums on marketable debt securities AccretionAmortizationOfDiscountsAndPremiumsInvestments $-1.46M USD 1 Quarter
Imputed interest income from licensing ImputedInterestIncomeFromLicensing $94.00K USD 1 Quarter
Imputed interest income from licensing ImputedInterestIncomeFromLicensing $70.00K USD 1 Quarter
Non-cash interest expense NonCashInterestExpense $54.00K USD 1 Quarter
Non-cash interest expense NonCashInterestExpense $-574.00K USD 1 Quarter
Other non-cash adjustments OtherNoncashIncomeExpense $52.00K USD 1 Quarter
Other non-cash adjustments OtherNoncashIncomeExpense $43.00K USD 1 Quarter
Accounts receivable IncreaseDecreaseInAccountsReceivable $-9.49M USD 1 Quarter
Accounts receivable IncreaseDecreaseInAccountsReceivable $-5.69M USD 1 Quarter
Prepaid expenses IncreaseDecreaseInPrepaidExpense $1.62M USD 1 Quarter
Prepaid expenses IncreaseDecreaseInPrepaidExpense $-210.00K USD 1 Quarter
Other current assets IncreaseDecreaseInOtherCurrentAssets $13.65M USD 1 Quarter
Other current assets IncreaseDecreaseInOtherCurrentAssets $-3.04M USD 1 Quarter
Operating lease right-of-use assets IncreaseDecreaseInOperatingLeaseRightOfUseAssets $-1.39M USD 1 Quarter
Operating lease right-of-use assets IncreaseDecreaseInOperatingLeaseRightOfUseAssets $-979.00K USD 1 Quarter
Other assets IncreaseDecreaseInOtherNoncurrentAssets $2.10M USD 1 Quarter
Other assets IncreaseDecreaseInOtherNoncurrentAssets $1.89M USD 1 Quarter
Accounts payable IncreaseDecreaseInAccountsPayableTrade $16.75M USD 1 Quarter
Accounts payable IncreaseDecreaseInAccountsPayableTrade $-3.10M USD 1 Quarter
Accrued expenses and other current liabilities IncreaseDecreaseInAccruedLiabilitiesAndOtherOperatingLiabilities $-15.44M USD 1 Quarter
Accrued expenses and other current liabilities IncreaseDecreaseInAccruedLiabilitiesAndOtherOperatingLiabilities $-26.47M USD 1 Quarter
Deferred revenue IncreaseDecreaseInDeferredRevenue $-433.00K USD 1 Quarter
Operating lease liabilities IncreaseDecreaseInOperatingLeaseLiabilities $1.01M USD 1 Quarter
Operating lease liabilities IncreaseDecreaseInOperatingLeaseLiabilities $-1.50M USD 1 Quarter
Other liabilities IncreaseDecreaseInOtherOperatingLiabilities $-2.85M USD 1 Quarter
Other liabilities IncreaseDecreaseInOtherOperatingLiabilities $6.93M USD 1 Quarter
Net cash used in operating activities NetCashProvidedByUsedInOperatingActivities $-80.92M USD 1 Quarter
Net cash used in operating activities NetCashProvidedByUsedInOperatingActivities $-55.91M USD 1 Quarter
Purchases of marketable debt securities PaymentsToAcquireMarketableSecurities $129.49M USD 1 Quarter
Maturities of marketable debt securities ProceedsFromSaleAndMaturityOfMarketableSecurities $49.86M USD 1 Quarter
Maturities of marketable debt securities ProceedsFromSaleAndMaturityOfMarketableSecurities $67.91M USD 1 Quarter
Purchases of property and equipment PaymentsToAcquirePropertyPlantAndEquipment $4.82M USD 1 Quarter
Purchases of property and equipment PaymentsToAcquirePropertyPlantAndEquipment $10.97M USD 1 Quarter
Net cash provided by (used in) investing activities NetCashProvidedByUsedInInvestingActivities $63.09M USD 1 Quarter
Net cash provided by (used in) investing activities NetCashProvidedByUsedInInvestingActivities $-90.59M USD 1 Quarter
Proceeds from exercise of stock options ProceedsFromStockOptionsExercised $471.00K USD 1 Quarter
Proceeds from exercise of stock options ProceedsFromStockOptionsExercised $337.00K USD 1 Quarter
Taxes paid related to net settlement of stock-based awards TaxesPaidRelatedToNetSettlementOfStockBasedAwards $419.00K USD 1 Quarter
Taxes paid related to net settlement of stock-based awards TaxesPaidRelatedToNetSettlementOfStockBasedAwards $284.00K USD 1 Quarter
Proceeds from issuance of common stock under employee stock purchase plan ProceedsFromIssuanceOfSharesUnderIncentiveAndShareBasedCompensationPlans $622.00K USD 1 Quarter
Proceeds from issuance of common stock under employee stock purchase plan ProceedsFromIssuanceOfSharesUnderIncentiveAndShareBasedCompensationPlans $583.00K USD 1 Quarter
Repayments under liability related to sale of future royalties, net of imputed interest RepaymentsUnderLiabilityRelatedToSaleOfFutureRoyalties $9.67M USD 1 Quarter
Repayments under liability related to sale of future royalties, net of imputed interest RepaymentsUnderLiabilityRelatedToSaleOfFutureRoyalties $7.51M USD 1 Quarter
Net cash used in financing activities NetCashProvidedByUsedInFinancingActivities $-6.83M USD 1 Quarter
Net cash used in financing activities NetCashProvidedByUsedInFinancingActivities $-9.04M USD 1 Quarter
Net decrease in cash and cash equivalents and restricted cash CashCashEquivalentsRestrictedCashAndRestrictedCashEquivalentsPeriodIncreaseDecreaseIncludingExchangeRateEffect $-153.34M USD 1 Quarter
Net decrease in cash and cash equivalents and restricted cash CashCashEquivalentsRestrictedCashAndRestrictedCashEquivalentsPeriodIncreaseDecreaseIncludingExchangeRateEffect $-26.86M USD 1 Quarter
Beginning of period CashCashEquivalentsRestrictedCashAndRestrictedCashEquivalentsIncludingDisposalGroupAndDiscontinuedOperations $193.90M USD Point-in-time
Beginning of period CashCashEquivalentsRestrictedCashAndRestrictedCashEquivalentsIncludingDisposalGroupAndDiscontinuedOperations $347.24M USD Point-in-time
Beginning of period CashCashEquivalentsRestrictedCashAndRestrictedCashEquivalentsIncludingDisposalGroupAndDiscontinuedOperations $72.12M USD Point-in-time
Beginning of period CashCashEquivalentsRestrictedCashAndRestrictedCashEquivalentsIncludingDisposalGroupAndDiscontinuedOperations $98.98M USD Point-in-time
End of period CashCashEquivalentsRestrictedCashAndRestrictedCashEquivalentsIncludingDisposalGroupAndDiscontinuedOperations $193.90M USD Point-in-time
End of period CashCashEquivalentsRestrictedCashAndRestrictedCashEquivalentsIncludingDisposalGroupAndDiscontinuedOperations $347.24M USD Point-in-time
End of period CashCashEquivalentsRestrictedCashAndRestrictedCashEquivalentsIncludingDisposalGroupAndDiscontinuedOperations $72.12M USD Point-in-time
End of period CashCashEquivalentsRestrictedCashAndRestrictedCashEquivalentsIncludingDisposalGroupAndDiscontinuedOperations $98.98M USD Point-in-time
Stockholders Equity 20 line items
Line Item Tag Value Unit Period
Balances StockholdersEquity $689.67M USD Point-in-time
Balances StockholdersEquity $516.20M USD Point-in-time
Balances StockholdersEquity $764.30M USD Point-in-time
Balances StockholdersEquity $465.14M USD Point-in-time
Vesting of restricted stock units, net of tax VestingOfRestrictedStockUnits $-284.00K USD 1 Quarter
Vesting of restricted stock units, net of tax VestingOfRestrictedStockUnits $-419.00K USD 1 Quarter
Exercise of stock options, net of tax StockIssuedDuringPeriodValueStockOptionsExercised $337.00K USD 1 Quarter
Exercise of stock options, net of tax StockIssuedDuringPeriodValueStockOptionsExercised $471.00K USD 1 Quarter
Issuance of common stock under employee stock purchase plan StockIssuedDuringPeriodValueEmployeeStockPurchasePlan $583.00K USD 1 Quarter
Issuance of common stock under employee stock purchase plan StockIssuedDuringPeriodValueEmployeeStockPurchasePlan $622.00K USD 1 Quarter
Stock-based compensation expense AdjustmentsToAdditionalPaidInCapitalSharebasedCompensationRequisiteServicePeriodRecognitionValue $10.80M USD 1 Quarter
Stock-based compensation expense AdjustmentsToAdditionalPaidInCapitalSharebasedCompensationRequisiteServicePeriodRecognitionValue $11.21M USD 1 Quarter
Unrealized gain (loss) on available-for-sale securities, net OtherComprehensiveIncomeLossAvailableForSaleSecuritiesAdjustmentNetOfTax $-9.38M USD 1 Quarter
Unrealized gain (loss) on available-for-sale securities, net OtherComprehensiveIncomeLossAvailableForSaleSecuritiesAdjustmentNetOfTax $3.78M USD 1 Quarter
Net loss NetIncomeLoss $-66.68M USD 1 Quarter
Net loss NetIncomeLoss $-76.72M USD 1 Quarter
Balances StockholdersEquity $689.67M USD Point-in-time
Balances StockholdersEquity $516.20M USD Point-in-time
Balances StockholdersEquity $764.30M USD Point-in-time
Balances StockholdersEquity $465.14M USD Point-in-time

Data is extracted from SEC EDGAR XBRL filings. Values shown are as reported in the filing.

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